Vivet Therapeutics

Very nice video explaining the potential of gene therapies:
https://www.youtube.com/watch?v=I69wPeDe-Cc

Gene Therapy Treatment Update - Platforms of Hope Learn more about the impact on rare disease diagnosis for conditions with a genetic component, and the potential to target a disease at its basis. Dr. P.J. ...

is a rare, progressive genetic disorder that causes excess copper to be stored in the body. Learn more about , Vivet Therapeutics-sponsored clinical trial and our , VTX-801:
www.gatewaytrialwilsondisease.com
This trial is taking place at several clinical sites across the United States and Europe.

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We are posting photos of Big Wows from the past, remembering the fun we had and honoring our volunteers. If you have one you want posted email it to [email protected]

Do you miss the t-shirts? What year was this?

VTX-801 Receives U.S. FDA Fast Track Designation for the Treatment of Wilson Disease | pfpfizeruscom Paris, France and New York, NY, August 12, 2021 – Vivet Therapeutics (“Vivet”), a clinical-stage biotechnology company, and Pfizer Inc. (NYSE: PFE) today announced the U.S. Food and Drug Administration (FDA) has granted Fast Track designation to VTX-801, Vivet’s clinical-stage gene therapy f...

Learn how aims to target the cause of by delivering a working ATP7B gene into cells. are now open for this investigational therapy. https://bit.ly/3hk1geX

Disease Treatments | ASGCT - American Society of Gene & Cell Therapy | Wilson disease is a rare genetic disorder that causes excess copper to be stored in the body. The disease is progressive, and if left untreated, can cause liver disease, brain injury, and premature death. Learn how gene therapy may target the cause of disease to slow or stop its progression, along w...

Pregnancy and Wilson Disease Women with Wilson disease who are pregnant - or are contemplating the safety of becoming pregnant - have many questions. Dr. Peter Ott addresses common ques...

Congratulations to all Women in Gene Therapy and to Dr. Gloria González-Aseguinolaza our CSO Therapeutics!👏
Very proud of our team, with 70% of women at Vivet ! 💪
https://www.liebertpub.com/doi/pdf/10.1089/hum.2021.29155.jea

Please share this link with everyone affected by Wilson disease. It is a 15 question survey to help the WDA create programming on diet and nutrition.

https://mailchi.mp/wilsonsdisease.org/new-educational-programming-with-your-survey-responses

Behind the Mystery: Wilson Disease - The Balancing Act Wilson disease is a rare, chronic disorder characterized by copper accumulation in organs and tissues that, if left untreated, may result in liver, neurologic, and psychiatric symptoms that progress over time. To understand more about how this disease affects patients, we met with Ed, who waited ove...

Vivet Therapeutics updated their website address.