Sarepta Therapeutics, Cambridge, MA Videos

Videos by Sarepta Therapeutics in Cambridge. Developing potentially life-changing precision genetic medicines for rare conditions. U.S. residents.

September is #NewbornScreeningAwarenessMonth! Learn about the progress in expanding newborn screening to include Duchenne. It’s a crucial step to eliminate diagnostic delays. We applaud efforts to expand screening in more states. #Duchenne #NBS

Other Sarepta Therapeutics videos

September is #NewbornScreeningAwarenessMonth! Learn about the progress in expanding newborn screening to include Duchenne. It’s a crucial step to eliminate diagnostic delays. We applaud efforts to expand screening in more states. #Duchenne #NBS

Find out where our latest FDA-approved treatment option for Duchenne is available: https://bit.ly/3tvUCwn

Nick and Agnes, whose son lives with Duchenne, share what in-school support and accommodations have made a difference for their son. Prepare for back to school here: https://bit.ly/4dNrJy9

Not many people are aware of the access challenges that can take place in accessing treatment. Our SareptAssist team not only understands your challenges, but is dedicated to helping you find the right answers and solutions as quickly as possible. Learn more: https://bit.ly/457JItK For U.S. Residents

“When Darren was diagnosed, he was two years and ten months. We had never heard the word Duchenne.” Discover the early signs of Duchenne: https://bit.ly/44Rfcp6

Find out if gene therapy could be right for your son, locate treatment centers in your area: https://bit.ly/3tvUCwn

What is the goal of gene therapy? How does it work? What is the latest information available? These questions and more are important to understand as you prepare for conversations with your doctor. Download the Gene Therapy Doctor Discussion Guide for a list of questions to consider discussing with your child’s doctor: https://bit.ly/3VCoPDR

From understanding how gene therapy works to learning about possible Duchenne clinical trials, this Gene Therapy Doctor Discussion Guide can help your family explore and learn more from speaking with your doctor: https://bit.ly/3VCoPDR

Our dedicated SareptAssist team is here to support your Duchenne journey every step of the way. Watch below to learn about the resources and guidance your family can access after treatment. https://bit.ly/457JItK For U.S. Residents

Your child’s doctor is your best resource. Find informational materials to help you guide discussions about gene therapy with your healthcare provider: https://bit.ly/4bLBZpH

Staying up to date on the latest Duchenne developments doesn’t have to be a time-consuming task. Sign up to receive the most up-to-date information on potential therapies: https://bit.ly/4bLBZpH

Providing personalized care for families living with Duchenne is the foundation of our work. A dedicated Case Manager approaches every concern and challenge with the knowledge of your family dynamics and history. Learn more: https://bit.ly/457JItK For U.S. Residents

When learning about different treatment approaches for Duchenne, it can be difficult to know which questions to ask your doctor. This Gene Therapy Doctor Discussion Guide can help you start that conversation: https://bit.ly/3VCoPDR

Duchenne therapies are always evolving, which can make finding accurate and timely information feel like an overwhelming task. We’re here to help. Contact SareptAssist for custom guidance as your family starts their treatment journey: https://bit.ly/457JItK For U.S. Residents

We consider it a privilege and important responsibility to work with and get to know families navigating life with Duchenne. Learn more about our personalized resource called SareptAssist. Members of our team are available to answer your questions now at the Parent Project Muscular Dystrophy Annual Conference. Use the conference app to sign up for a 1:1 meeting. https://bit.ly/457JItK

If you’re at the Parent Project Muscular Dystrophy conference, you can sign up to meet with our SareptAssist team and get your questions answered by a qualified Duchenne Case Manager. Find a Sarepta team member at one of our booths or check the conference app to find out how to sign up.

Find possible treatment sites near you.
Interested in our newest treatment for Duchenne? See the locator map for possible treatment sites near you: https://bit.ly/3tvUCwn

What are the important topics to understand when evaluating whether gene therapy may be appropriate for your family? Use this Gene Therapy Doctor Discussion Guide to start the conversation with your child’s doctor: https://bit.ly/3VCoPDR

Sarepta - SareptAssist - Sarah 08 - Navigating New Therapies - V 3_Subs.mov
As treatment options evolve, so do our resources for Duchenne families. Our SareptAssist team is committed to answering all your questions about new developments and treatment options. Learn more: https://bit.ly/457JItK For U.S. Residents

Our head of R&D and Chief Scientific Officer, Louise Rodino-Klapac, PhD, on today’s news regarding advances in the treatment of Duchenne muscular dystrophy: