Sarepta Therapeutics
Developing potentially life-changing precision genetic medicines for rare conditions. U.S. residents.
September is ! Learn about the progress in expanding newborn screening to include Duchenne. It’s a crucial step to eliminate diagnostic delays. We applaud efforts to expand screening in more states.
Find out where our latest FDA-approved treatment option for Duchenne is available: https://bit.ly/3tvUCwn
08/29/2024
Important progress in newborn screening right here in our home state of Massachusetts. Duchenne was added to the state’s newborn screening panel as part of a broader maternal health plan, and Massachusetts now joins the other states that have taken this critical step.
We applaud state leadership for acting on this important health issue, commend ongoing efforts in additional states and ask federal leaders to follow suit and add screening for Duchenne nationwide. Because all babies deserve the opportunity for early diagnosis and intervention. https://bit.ly/4fZvG3E
08/28/2024
What does our gene therapy news mean? Learn how to connect with a SareptAssist Case Manager to get answers: https://bit.ly/3tvUCwn
Nick and Agnes, whose son lives with Duchenne, share what in-school support and accommodations have made a difference for their son. Prepare for back to school here: https://bit.ly/4dNrJy9
Not many people are aware of the access challenges that can take place in accessing treatment. Our SareptAssist team not only understands your challenges, but is dedicated to helping you find the right answers and solutions as quickly as possible. Learn more: https://bit.ly/457JItK
For U.S. Residents
08/19/2024
What does the newly expanded label of our latest Duchenne therapy mean? Talk to one of our SareptAssist Case Managers: https://bit.ly/3tvUCwn
“When Darren was diagnosed, he was two years and ten months. We had never heard the word Duchenne.” Discover the early signs of Duchenne: https://bit.ly/44Rfcp6
Find out if gene therapy could be right for your son, locate treatment centers in your area: https://bit.ly/3tvUCwn
08/09/2024
Independence has a different meaning for every person living with Duchenne, driven by personal goals and aspirations. For Kenan, independence is finding the balance between asking for help and tackling tasks by himself.
Read his full story in the latest issue of the SareptAssist newsletter.
08/07/2024
The FDA has expanded the approval of our gene therapy based on additional clinical trial data. Learn more: https://bit.ly/3tvUCwn
What is the goal of gene therapy? How does it work? What is the latest information available? These questions and more are important to understand as you prepare for conversations with your doctor. Download the Gene Therapy Doctor Discussion Guide for a list of questions to consider discussing with your child’s doctor: https://bit.ly/3VCoPDR
07/31/2024
Do you have questions about the recent news about broader access to our latest Duchenne therapy? Learn how to connect with us: https://bit.ly/3tvUCwn
From understanding how gene therapy works to learning about possible Duchenne clinical trials, this Gene Therapy Doctor Discussion Guide can help your family explore and learn more from speaking with your doctor: https://bit.ly/3VCoPDR
Our dedicated SareptAssist team is here to support your Duchenne journey every step of the way. Watch below to learn about the resources and guidance your family can access after treatment. https://bit.ly/457JItK
For U.S. Residents
07/24/2024
Learn about the label expansion, our latest advancement in treatment options for Duchenne. https://bit.ly/3tvUCwn
Your child’s doctor is your best resource. Find informational materials to help you guide discussions about gene therapy with your healthcare provider: https://bit.ly/4bLBZpH
07/19/2024
Today is the last day to apply for our 2024 LGMD grant program, an initiative that awards funds to organizations that can help drive LGMD awareness and education. Apply here: https://Sarepta.com/LGMDGrantAwardProgram
07/18/2024
Kenan, living with Duchenne, shares how he worked with his family and team of doctors to make more decisions about his care as he grew older. Read his full story in the latest issue of the SareptAssist newsletter.
07/17/2024
Because each gene therapy is different, it’s important to understand how gene therapies for Duchenne are unique. Check out the Gene Therapy Doctor Discussion Guide to inform what questions may be important to discuss with your child’s doctor.
Staying up to date on the latest Duchenne developments doesn’t have to be a time-consuming task. Sign up to receive the most up-to-date information on potential therapies: https://bit.ly/4bLBZpH
Providing personalized care for families living with Duchenne is the foundation of our work. A dedicated Case Manager approaches every concern and challenge with the knowledge of your family dynamics and history. Learn more: https://bit.ly/457JItK
For U.S. Residents
When learning about different treatment approaches for Duchenne, it can be difficult to know which questions to ask your doctor. This Gene Therapy Doctor Discussion Guide can help you start that conversation: https://bit.ly/3VCoPDR
07/08/2024
Greater awareness of LGMDs is needed. To support this, we’re once again offering our grant program to award funds to selected organizations that can help drive awareness and education. Learn how to apply: https://Sarepta.com/LGMDGrantAwardProgram
Duchenne therapies are always evolving, which can make finding accurate and timely information feel like an overwhelming task. We’re here to help. Contact SareptAssist for custom guidance as your family starts their treatment journey: https://bit.ly/457JItK
For U.S. Residents
07/03/2024
Whether you’re just beginning to learn about gene therapy or if you know a lot, the Gene Therapy Doctor Discussion Guide can help inform a conversation with your doctor.
07/01/2024
Talking to your doctor is the best way to get more detailed information about gene therapy. But knowing what to ask might feel difficult or overwhelming. Planning ahead can help you get the most out of a conversation with your child's doctor about treatment options for Duchenne. Download this guide to help you get started.
06/29/2024
Amazing time connecting with families and exploring the latest science at Parent Project Muscular Dystrophy’s Annual Conference. If you have more questions or if you want to be connected to additional resources, our Patient Advocacy team is here to help. DM us on social or email [email protected].
We consider it a privilege and important responsibility to work with and get to know families navigating life with Duchenne. Learn more about our personalized resource called SareptAssist. Members of our team are available to answer your questions now at the Parent Project Muscular Dystrophy Annual Conference. Use the conference app to sign up for a 1:1 meeting.
https://bit.ly/457JItK
06/28/2024
There are many ways to connect with Sarepta at Parent Project Muscular Dystrophy Annual Conference. Members of our Patient Advocacy, SareptAssist, Gene Therapy and Exon-skipping teams will be there! We look forward to meeting you.
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